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30 Nov 2017

Solid Biosciences Initiates Clinical Trial for Gene Transfer Candidate SGT-001 in Patients with Duchenne Muscular Dystrophy

Solid Biosciences is a life science company focused on solving Duchenne muscular dystrophy.

Cambridge, MA, November 30, 2017 , Solid   Biosciences.
Solid Biosciences announced today that it has initiated clinical trial activities for SGT-001, the company's lead microdystrophin gene transfer candidate for the treatment of Duchenne muscular dystrophy (DMD). The Phase I/II adaptive study, called IGNITE DMD, will evaluate the safety and efficacy of a single intravenous (IV) dose of SGT-001 in ambulatory and non-ambulatory adolescents and children with DMD. Enrollment will begin at the first clinical trial site in the United States in the coming days.

Read more about this  exciting  development in this  article from Solid Biosciences or at the link below. 
<https://solidbio.com/content/solid-biosciences-initiates-clinical-trial-gene-transfer-candidate-sgt-001-patients-duchenne>

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